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Driving Innovation.

Developing life-saving drugs for patients in need
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Life-saving drugs.

At OrphAI Therapeutics, we are focused on identifying and developing treatments for conditions with unmet medical need. Our current drug candidates target several disorders including Group 1 and Group 3 pulmonary hypertension, bronchiolitis obliterans post lung transplant, and SWI/SNF mutated or dysregulated cancers.

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